Louis-Armstrong

FDA OK’s Rare Metabolic Disorder Tx; Junk on the Big Screen

Lumasiran (Oxlumo), the first treatment ever for the rare metabolic disorder primary hyperoxaluria type 1, gained…

FDA Clears First Drug to Treat Ultra-Rare Metabolic Disorder

The US Food and Drug Administration (FDA) has approved lumasiran (Oxlumo, Alnylam Pharmaceuticals) subcutaneous injection to…